SURACE, Enrico Maria

SURACE, Enrico Maria  

DIPARTIMENTO DI SCIENZE MEDICHE TRASLAZIONALI  

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Risultati 1 - 20 di 72 (tempo di esecuzione: 0.035 secondi).
Titolo Tipologia Data di pubblicazione Autore(i) File
The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer. 1.1 Articolo in rivista 2005 Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J.
Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues. 1.1 Articolo in rivista 2001 Karakousis, Pc; John, Sk; Behling, Kc; Surace, Enrico Maria; Smith, Je; Hendrickson, A; Tang, Wx; Bennett, J; Milam, Ah
Pigment epithelium-derived factor expression in the developing mouse eye. 1.1 Articolo in rivista 2002 Behling, Kc; Surace, Enrico Maria; Bennett, J.
Adeno-associated viral vectors for retinal gene transfer. 1.1 Articolo in rivista 2003 Surace, Enrico Maria; Auricchio, Alberto
GENE THERAPY FOR LEBER'S CONGENITAL AMAUROSIS IS SAFE AND EFFECTIVE 1.5 YEARS AFTER VECTOR ADMINISTRATION 1.1 Articolo in rivista 2010 F., Simonelli; A. M., Maguire; F., Testa; E. A., Pierce; F., Mingozzi; J. L., Bennicelli; S., Rossi; K., Marshall; S., Banfi; Surace, Enrico Maria; J., Sun; T. M., Redmond; X., Zhu; K. S., Scindler; G. S., Ying; C., Ziviello; C., Acerra; J. F., Wright; J. W., Mcdonnell; K. A., High; J., Bennett; Auricchio, Alberto
Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1 1.1 Articolo in rivista 2000 Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea
Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium. 1.1 Articolo in rivista 2000 Surace, Enrico Maria; Angeletti, B; Ballabio, Andrea; Marigo, V.
Delivery of adeno-associated virus vectors to the fetal retina: impact of viral capsid proteins on retinal neuronal progenitor transduction. 1.1 Articolo in rivista 2003 Surace, Enrico Maria; Auricchio, Alberto; Reich, Sj; Rex, T; Glover, E; Pineles, S; Tang, W; O'Connor, E; Lyubarsky, A; Savchenko, A; Pugh EN, Jr; Maguire, Am; Wilson, Jm; Bennett, J.
Systemic but not intraocular Epo gene transfer protects the retina from light- and genetic-induced degeneration. 1.1 Articolo in rivista 2004 Rex, T. S.; M. ALLOCCA, M.; Domenici, L.; Surace, Enrico Maria; Maguire, A. M.; Lyubarsky, A.; Cellerino, A.; Bennett, J.; Auricchio, Alberto
Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration. 1.1 Articolo in rivista 2010 Simonelli, F; Maguire, Am; Testa, F; Pierce, Ea; Mingozzi, F; Bennicelli, Jl; Rossi, S; Marshall, K; Banfi, S; Surace, Enrico Maria; Sun, J; Redmond, Tm; Zhu, X; Shindler, Ks; Ying, Gs; Ziviello, C; Acerra, C; Wright, Jf; Mcdonnell, Jw; High, Ka; Bennett, J; Auricchio, Alberto
The ocular albinism type 1 (OA1) gene controls melanosome maturation and size. 1.1 Articolo in rivista 2005 Cortese, K; Giordano, F; Surace, Enrico Maria; Venturi, C; Ballabio, Andrea; Tacchetti, C; Marigo, V.
SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein-associated amino acid transporter family. 1.1 Articolo in rivista 1999 Bassi, Mt; Sperandeo, Mp; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De Grandi, A; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G.
The Ocular Albinism type 1 (OA!) gene controls melanosome maturation and size. 1.1 Articolo in rivista 2005 Cortese, K; Giordano, F; Surace, Enrico Maria; Venturi, C; Ballabio, Andrea; Tacchetti, C; AND MARIGO, V.
The ocular albinism type 1 (OA1) protein, an intracellur G protein-coupled receptor, regulates melanosome transport in pigment cells. 1.1 Articolo in rivista 2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, P; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, M. V.
AAV vectors efficiently and stably transduce fetal retina. 1.1 Articolo in rivista 2003 Surace, Enrico Maria; Auricchio, Alberto; Reich, S. J.; Rex, T.; Glover, E.; Pineles, S.; Tang, W.; O’Connor, E.; Lyubarsky, A.; Savchenko, A.; Pugh, E.; Maguire, A. WILSON J. M. BENNETT J.
Zinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosa 1.1 Articolo in rivista 2011 C., Mussolino; D., Sanges; E., Marrocco; C., Bonetti; U., Di Vicino; V., Marigo; Auricchio, Alberto; G., Meroni; Surace, Enrico Maria
AAV-mediated photoreceptor transduction of the pig cone-enriched retina 1.1 Articolo in rivista 2011 C., Mussolino; M., Della Corte; S., Rossi; F., Viola; U., Di Vicino; E., Marrocco; S., Neglia; M., Doria; F., Testa; R., Giovannoni; M., Crasta; M., Giunti; E., Villani; M., Lavitrano; M. L., Bacci; R., Ratiglia; F., Simonelli; Auricchio, Alberto; Surace, Enrico Maria
TOWARDS CLINICAL TRIALS FOR AAV-MEDIATED EYE- AND LIVER - DIRECT GENE THERAPY TRANSLATION AAV 8.07 Progetti di Ricerca Finanziati 2011 Auricchio, Alberto; Surace, Enrico Maria; BRUNETTI PIERRI, Nicola
SLC7A8, a gene mapping within the lysinuric protein intolerance critical region, encodes a new member of the glycoprotein associated amino acid transporter family. 1.1 Articolo in rivista 1999 Bassi, M. T.; Sperandeo, M. P.; Incerti, B; Bulfone, A; Pepe, A; Surace, Enrico Maria; Gattuso, C; De, Grandi; A, ; Buoninconti, A; Riboni, M; Manzoni, M; Andria, G; Ballabio, Andrea; Borsani, G; Sebastio, G.
AP20817-inducible activation of chimeric insulin receptor mimics insulin action in hepatocytes transduced with AAV 4.1 Articoli in Atti di convegno 2004 Auricchio, Alberto; G., Cotugno; Formisano, Pietro; Beguinot, Francesco; Surace, Enrico Maria; R., Pollock