SURACE, Enrico Maria
SURACE, Enrico Maria
DIPARTIMENTO DI SCIENZE MEDICHE TRASLAZIONALI
Adeno-associated viral vectors for retinal gene transfer.
2003 Surace, Enrico Maria; Auricchio, Alberto
The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer.
2005 Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J.
Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues.
2001 Karakousis, Pc; John, Sk; Behling, Kc; Surace, Enrico Maria; Smith, Je; Hendrickson, A; Tang, Wx; Bennett, J; Milam, Ah
Pigment epithelium-derived factor expression in the developing mouse eye.
2002 Behling, Kc; Surace, Enrico Maria; Bennett, J.
Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium.
2000 Surace, Enrico Maria; Angeletti, B; Ballabio, Andrea; Marigo, V.
Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1
2000 Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea
TOWARDS CLINICAL TRIALS FOR AAV-MEDIATED EYE- AND LIVER - DIRECT GENE THERAPY TRANSLATION AAV
2011 Auricchio, Alberto; Surace, Enrico Maria; BRUNETTI PIERRI, Nicola
AAV vectors efficiently and stably transduce fetal retina.
2003 Surace, Enrico Maria; Auricchio, Alberto; Reich, S. J.; Rex, T.; Glover, E.; Pineles, S.; Tang, W.; O’Connor, E.; Lyubarsky, A.; Savchenko, A.; Pugh, E.; Maguire, A. WILSON J. M. BENNETT J.
The ocular albinism type 1 (OA1) G-protein-coupled receptor functions with MART-1 at early stages of melanogenesis to control melanosome identity and composition.
2009 Giordano, F; Bonetti, C; Surace, Enrico Maria; Marigo, V; Raposo, G.
Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by morpholino antisense oligonucleotides.
2006 Vetrini, F; Tammaro, R; Bondanza, S; Surace, Enrico Maria; Auricchio, Alberto; De Luca, M; Ballabio, Andrea; Marigo, V.
Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer.
2005 Surace, Enrico Maria; Domenici, L; Cortese, K; Cotugno, G; Di Vicino, U; Venturi, C; Cellerino, A; Marigo, V; Tacchetti, C; Ballabio, Andrea; Auricchio, Alberto
The ocular albinism type 1 (OA1) gene controls melanosome maturation and size.
2005 Cortese, K; Giordano, F; Surace, Enrico Maria; Venturi, C; Ballabio, Andrea; Tacchetti, C; Marigo, V.
The long noncoding RNA Vax2os1 controls the cell cycle progression of photoreceptor progenitors in the mouse retina.
2012 Meola, N; Pizzo, M; Alfano, G; Surace, Enrico Maria; Banfi, S.
Molecular and clinical characterization of albinism in a large cohort of Italian patients.
2011 Gargiulo, A; Testa, F; Rossi, S; Di Iorio, V; Fecarotta, S; DE BERARDINIS, Teresa; Iovine, A; Magli, A; Signorini, S; Fazzi, E; Galantuomo, Ms; Fossarello, M; Montefusco, S; Ciccodicola, A; Neri, A; Macaluso, C; Simonelli, F; Surace, Enrico Maria
Mouse embryonic retina delivers information controlling cortical neurogenesis.
2010 Bonetti, C; Surace, Enrico Maria
Systemic but not intraocular Epo gene transfer protects the retina from light-and genetic-induced degeneration.
2004 Rex, Ts; Allocca, M; Domenici, L; Surace, Enrico Maria; Maguire, Am; Lyubarsky, A; Cellerino, A; Bennett, J; Auricchio, Alberto
In utero gene therapy rescues vision in a murine model of congenital blindness.
2004 Dejneka, Ns; Surace, Enrico Maria; Aleman, Ts; Cideciyan, Av; Lyubarsky, A; Savchenko, A; Redmond, Tm; Tang, W; Wei, Z; Rex, Ts; Glover, E; Maguire, Am; Pugh EN, Jr; Jacobson, Sg; Bennett, J.
Safety and efficacy of gene transfer for Leber's congenital amaurosis.
2008 Maguire, Am; Simonelli, F; Pierce, Ea; Pugh EN, Jr; Mingozzi, F; Bennicelli, J; Banfi, S; Marshall, Ka; Testa, F; Surace, Enrico Maria; Rossi, S; Lyubarsky, A; Arruda, Vr; Konkle, B; Stone, E; Sun, J; Jacobs, J; Dell'Osso, L; Hertle, R; Ma, Jx; Redmond, Tm; Zhu, X; Hauck, B; Zelenaia, O; Shindler, Ks; Maguire, Mg; Wright, Jf; Volpe, Nj; Mcdonnell, Jw; Auricchio, Alberto; High, Ka; Bennett, J.
The ocular albinism type 1 protein, an intracellular G protein-coupled receptor, regulates melanosome transport in pigment cells.
2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, G; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, Mv
Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina.
2013 Puppo, A; Bello, A; Manfredi, A; Cesi, G; Marrocco, E; Della Corte, M; Rossi, S; Giunti, M; Bacci, Ml; Simonelli, F; Surace, Enrico Maria; Kobinger, Gp; Auricchio, Alberto
| Titolo | Tipologia | Data di pubblicazione | Autore(i) | File |
|---|---|---|---|---|
| Adeno-associated viral vectors for retinal gene transfer. | 1.1 Articolo in rivista | 2003 | Surace, Enrico Maria; Auricchio, Alberto | |
| The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer. | 1.1 Articolo in rivista | 2005 | Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J. | |
| Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues. | 1.1 Articolo in rivista | 2001 | Karakousis, Pc; John, Sk; Behling, Kc; Surace, Enrico Maria; Smith, Je; Hendrickson, A; Tang, Wx; Bennett, J; Milam, Ah | |
| Pigment epithelium-derived factor expression in the developing mouse eye. | 1.1 Articolo in rivista | 2002 | Behling, Kc; Surace, Enrico Maria; Bennett, J. | |
| Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium. | 1.1 Articolo in rivista | 2000 | Surace, Enrico Maria; Angeletti, B; Ballabio, Andrea; Marigo, V. | |
| Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1 | 1.1 Articolo in rivista | 2000 | Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea | |
| TOWARDS CLINICAL TRIALS FOR AAV-MEDIATED EYE- AND LIVER - DIRECT GENE THERAPY TRANSLATION AAV | 8.07 Progetti di Ricerca Finanziati | 2011 | Auricchio, Alberto; Surace, Enrico Maria; BRUNETTI PIERRI, Nicola | |
| AAV vectors efficiently and stably transduce fetal retina. | 1.1 Articolo in rivista | 2003 | Surace, Enrico Maria; Auricchio, Alberto; Reich, S. J.; Rex, T.; Glover, E.; Pineles, S.; Tang, W.; O’Connor, E.; Lyubarsky, A.; Savchenko, A.; Pugh, E.; Maguire, A. WILSON J. M. BENNETT J. | |
| The ocular albinism type 1 (OA1) G-protein-coupled receptor functions with MART-1 at early stages of melanogenesis to control melanosome identity and composition. | 1.1 Articolo in rivista | 2009 | Giordano, F; Bonetti, C; Surace, Enrico Maria; Marigo, V; Raposo, G. | |
| Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by morpholino antisense oligonucleotides. | 1.1 Articolo in rivista | 2006 | Vetrini, F; Tammaro, R; Bondanza, S; Surace, Enrico Maria; Auricchio, Alberto; De Luca, M; Ballabio, Andrea; Marigo, V. | |
| Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer. | 1.1 Articolo in rivista | 2005 | Surace, Enrico Maria; Domenici, L; Cortese, K; Cotugno, G; Di Vicino, U; Venturi, C; Cellerino, A; Marigo, V; Tacchetti, C; Ballabio, Andrea; Auricchio, Alberto | |
| The ocular albinism type 1 (OA1) gene controls melanosome maturation and size. | 1.1 Articolo in rivista | 2005 | Cortese, K; Giordano, F; Surace, Enrico Maria; Venturi, C; Ballabio, Andrea; Tacchetti, C; Marigo, V. | |
| The long noncoding RNA Vax2os1 controls the cell cycle progression of photoreceptor progenitors in the mouse retina. | 1.1 Articolo in rivista | 2012 | Meola, N; Pizzo, M; Alfano, G; Surace, Enrico Maria; Banfi, S. | |
| Molecular and clinical characterization of albinism in a large cohort of Italian patients. | 1.1 Articolo in rivista | 2011 | Gargiulo, A; Testa, F; Rossi, S; Di Iorio, V; Fecarotta, S; DE BERARDINIS, Teresa; Iovine, A; Magli, A; Signorini, S; Fazzi, E; Galantuomo, Ms; Fossarello, M; Montefusco, S; Ciccodicola, A; Neri, A; Macaluso, C; Simonelli, F; Surace, Enrico Maria | |
| Mouse embryonic retina delivers information controlling cortical neurogenesis. | 1.1 Articolo in rivista | 2010 | Bonetti, C; Surace, Enrico Maria | |
| Systemic but not intraocular Epo gene transfer protects the retina from light-and genetic-induced degeneration. | 1.1 Articolo in rivista | 2004 | Rex, Ts; Allocca, M; Domenici, L; Surace, Enrico Maria; Maguire, Am; Lyubarsky, A; Cellerino, A; Bennett, J; Auricchio, Alberto | |
| In utero gene therapy rescues vision in a murine model of congenital blindness. | 1.1 Articolo in rivista | 2004 | Dejneka, Ns; Surace, Enrico Maria; Aleman, Ts; Cideciyan, Av; Lyubarsky, A; Savchenko, A; Redmond, Tm; Tang, W; Wei, Z; Rex, Ts; Glover, E; Maguire, Am; Pugh EN, Jr; Jacobson, Sg; Bennett, J. | |
| Safety and efficacy of gene transfer for Leber's congenital amaurosis. | 1.1 Articolo in rivista | 2008 | Maguire, Am; Simonelli, F; Pierce, Ea; Pugh EN, Jr; Mingozzi, F; Bennicelli, J; Banfi, S; Marshall, Ka; Testa, F; Surace, Enrico Maria; Rossi, S; Lyubarsky, A; Arruda, Vr; Konkle, B; Stone, E; Sun, J; Jacobs, J; Dell'Osso, L; Hertle, R; Ma, Jx; Redmond, Tm; Zhu, X; Hauck, B; Zelenaia, O; Shindler, Ks; Maguire, Mg; Wright, Jf; Volpe, Nj; Mcdonnell, Jw; Auricchio, Alberto; High, Ka; Bennett, J. | |
| The ocular albinism type 1 protein, an intracellular G protein-coupled receptor, regulates melanosome transport in pigment cells. | 1.1 Articolo in rivista | 2008 | Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, G; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, Mv | |
| Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina. | 1.1 Articolo in rivista | 2013 | Puppo, A; Bello, A; Manfredi, A; Cesi, G; Marrocco, E; Della Corte, M; Rossi, S; Giunti, M; Bacci, Ml; Simonelli, F; Surace, Enrico Maria; Kobinger, Gp; Auricchio, Alberto |