SURACE, Enrico Maria

SURACE, Enrico Maria  

DIPARTIMENTO DI SCIENZE MEDICHE TRASLAZIONALI  

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Risultati 1 - 20 di 74 (tempo di esecuzione: 0.031 secondi).
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Adeno-associated viral vectors for retinal gene transfer. 1.1 Articolo in rivista 2003 Surace, Enrico Maria; Auricchio, Alberto
The distribution, concentration, and toxicity of enhanced green fluorescent protein in retinal cells after genomic or somatic (virus-mediated) gene transfer. 1.1 Articolo in rivista 2005 Rex, Ts; Peet, Ja; Surace, Enrico Maria; Calvert, Pd; Nikonov, Ss; Lyubarsky, Al; Bendo, E; Hughes, T; Pugh EN, Jr; Bennett, J.
Localization of pigment epithelium derived factor (PEDF) in developing and adult human ocular tissues. 1.1 Articolo in rivista 2001 Karakousis, Pc; John, Sk; Behling, Kc; Surace, Enrico Maria; Smith, Je; Hendrickson, A; Tang, Wx; Bennett, J; Milam, Ah
Pigment epithelium-derived factor expression in the developing mouse eye. 1.1 Articolo in rivista 2002 Behling, Kc; Surace, Enrico Maria; Bennett, J.
GENE THERAPY FOR LEBER'S CONGENITAL AMAUROSIS IS SAFE AND EFFECTIVE 1.5 YEARS AFTER VECTOR ADMINISTRATION 1.1 Articolo in rivista 2010 F., Simonelli; A. M., Maguire; F., Testa; E. A., Pierce; F., Mingozzi; J. L., Bennicelli; S., Rossi; K., Marshall; S., Banfi; Surace, Enrico Maria; J., Sun; T. M., Redmond; X., Zhu; K. S., Scindler; G. S., Ying; C., Ziviello; C., Acerra; J. F., Wright; J. W., Mcdonnell; K. A., High; J., Bennett; Auricchio, Alberto
Expression pattern of the ocular albinism type 1 (Oa1) gene in the murine retinal pigment epithelium. 1.1 Articolo in rivista 2000 Surace, Enrico Maria; Angeletti, B; Ballabio, Andrea; Marigo, V.
Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1 1.1 Articolo in rivista 2000 Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea
Oa1 knock-out: new insights on the pathogenesis of ocular albinism type 1. 1.1 Articolo in rivista 2000 Incerti, B; Cortese, K; Pizzigoni, A; Surace, Enrico Maria; Varani, S; Coppola, M; Jeffery, G; Seeliger, M; Jaissle, G; Bennett, Dc; Marigo, V; Schiaffino, Mv; Tacchetti, C; Ballabio, Andrea
The ocular albinism type 1 (OA1) G-protein-coupled receptor functions with MART-1 at early stages of melanogenesis to control melanosome identity and composition. 1.1 Articolo in rivista 2009 Giordano, F; Bonetti, C; Surace, Enrico Maria; Marigo, V; Raposo, G.
Systemic but not intraocular Epo gene transfer protects the retina from light-and genetic-induced degeneration. 1.1 Articolo in rivista 2004 Rex, Ts; Allocca, M; Domenici, L; Surace, Enrico Maria; Maguire, Am; Lyubarsky, A; Cellerino, A; Bennett, J; Auricchio, Alberto
Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by morpholino antisense oligonucleotides. 1.1 Articolo in rivista 2006 Vetrini, F; Tammaro, R; Bondanza, S; Surace, Enrico Maria; Auricchio, Alberto; De Luca, M; Ballabio, Andrea; Marigo, V.
Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer. 1.1 Articolo in rivista 2005 Surace, Enrico Maria; Domenici, L; Cortese, K; Cotugno, G; Di Vicino, U; Venturi, C; Cellerino, A; Marigo, V; Tacchetti, C; Ballabio, Andrea; Auricchio, Alberto
The ocular albinism type 1 (OA1) protein, an intracellur G protein-coupled receptor, regulates melanosome transport in pigment cells. 1.1 Articolo in rivista 2008 Palmisano, I; Bagnato, P; Palmigiano, A; Innamorati, P; Rotondo, G; Altimare, D; Venturi, C; Sviderskaya, Ev; Piccirillo, R; Coppola, M; Marigo, V; Incerti, B; Ballabio, Andrea; Surace, Enrico Maria; Tacchetti, C; Bennett, Dc; Schiaffino, M. V.
Systemic but not intraocular Epo gene transfer protects the retina from light- and genetic-induced degeneration. 1.1 Articolo in rivista 2004 Rex, T. S.; M. ALLOCCA, M.; Domenici, L.; Surace, Enrico Maria; Maguire, A. M.; Lyubarsky, A.; Cellerino, A.; Bennett, J.; Auricchio, Alberto
Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2. 1.1 Articolo in rivista 2013 Testa, F; Maguire, Am; Rossi, S; Pierce, Ea; Melillo, P; Marshall, K; Banfi, S; Surace, Enrico Maria; Sun, J; Acerra, C; Wright, Jf; Wellman, J; High, Ka; Auricchio, Alberto; Bennett, J; Simonelli, F.
Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina. 1.1 Articolo in rivista 2013 Puppo, A; Bello, A; Manfredi, A; Cesi, G; Marrocco, E; Della Corte, M; Rossi, S; Giunti, M; Bacci, Ml; Simonelli, F; Surace, Enrico Maria; Kobinger, Gp; Auricchio, Alberto
Safety and efficacy of gene transfer for Leber's congenital amaurosis. 1.1 Articolo in rivista 2008 Maguire, Am; Simonelli, F; Pierce, Ea; Pugh EN, Jr; Mingozzi, F; Bennicelli, J; Banfi, S; Marshall, Ka; Testa, F; Surace, Enrico Maria; Rossi, S; Lyubarsky, A; Arruda, Vr; Konkle, B; Stone, E; Sun, J; Jacobs, J; Dell'Osso, L; Hertle, R; Ma, Jx; Redmond, Tm; Zhu, X; Hauck, B; Zelenaia, O; Shindler, Ks; Maguire, Mg; Wright, Jf; Volpe, Nj; Mcdonnell, Jw; Auricchio, Alberto; High, Ka; Bennett, J.
Inhibition of ocular neovascularization by Hedgehog blockade. 1.1 Articolo in rivista 2006 Surace, Enrico Maria; Balaggan, K. S.; Tessitore, A.; Mussolino, C.; Cotugno, G.; Bonetti, C.; Vitale, A.; Ali, R. R.; Auricchio, Alberto
AAV-mediated Tyrosinase Gene Transfer Restores Melanogenesis and Retinal Function in a Model of Oculo-cutaneous Albinism Type I (OCA1). 1.1 Articolo in rivista 2009 A., Gargiulo; C., Bonetti; S., Montefusco; S., Neglia; U., Di Vicino; E., Marrocco; Md, Corte; L., Domenici; Auricchio, Alberto; Surace, Enrico Maria
Versatility of AAV vectors for retinal gene transfer 1.1 Articolo in rivista 2008 Surace, Enrico Maria; Auricchio, Alberto